A61K48/00
Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
A61K48/00
Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
A61K48/005
characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
A61K48/005
characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
A61K48/0066
Manipulation of the nucleic acid to modify its expression pattern, e.g. enhance its duration of expression, achieved by the presence of particular introns in the delivered nucleic acid
A61K48/0066
Manipulation of the nucleic acid to modify its expression pattern, e.g. enhance its duration of expression, achieved by the presence of particular introns in the delivered nucleic acid