Patent classifications
C
CHEMISTRY; METALLURGY
Load children
C12
BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
Load children
C12Y
ENZYMES
Load children
306/00
Hydrolases acting on acid anhydrides (3.6)
Load children Filter patents View analytics View as hierarchy Open in page
C12Y306/01
in phosphorus-containing anhydrides (3.6.1)
Load children Filter patents View analytics View as hierarchy Open in page
C12Y306/01059
m7GpppX diphosphatase (3.6.1.59)
Filter patents View analytics View as hierarchy Open in page

C12Y306/01059

COMPOSITIONS FOR INCREASING SURVIVAL OF MOTOR NEURON PROTEIN (SMN) LEVELS IN TARGET CELLS AND METHODS OF USE THEREOF FOR THE TREATMENT OF SPINAL MUSCULAR ATROPHY
20170355956 · 2017-12-14 ·

Compositions for altering splicing activity of the DcpS gene and increasing SMN protein expression in target cells are provided. Also disclosed are methods of use of such compositions for the treatment of SMA.